婴儿型庞贝病患儿超说明书应用阿糖苷酶α的药学监护1例
杨丹丹, 袁丽华, 孙尧, 曾缘缘
Pharmaceutical care for off-label use of alglucosidase alfa in an infant with infantile-onset Pompe disease: a case report
YANG Dandan, YUAN Lihua, SUN Yao, ZENG Yuanyuan
中国医院药学杂志
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2026, (14): 1706
-1710
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DOI: 10.13286/j.1001-5213.2026.14.16